Orphidis focuses on innovative therapies where treatment is specialist-led and patient identification, access and execution at the right treatment centres are critical.
Small, often underdiagnosed populations where patient identification and access are central.
Innovative cancer therapies delivered through specialist centres and hospital access pathways
Hospital-administered and high-value therapies where specialist prescribing and access determine uptake
Patients may be treated in a limited number of specialist centres, making precision more important than commercial scale
Finding the right patients and understanding diagnosis and referral pathways can matter as much as product awareness
Registration alone does not guarantee access. Reimbursement, private funding, hospital processes and named-patient pathways all influence how a medicine reaches patients
Resources go where they matter most: the centres, physicians and access pathways that determine treatment
Estimate based on a global rare-disease prevalence of 3.5–5.9% applied to approximately 2.5 billion people. Sources: Nguengang Wakap et al., European Journal of Human Genetics (2020); UN World Population Prospects 2024.
Whether you are considering managed access, registration or broader commercialisation, we’d welcome a conversation.