Focused on specialist medicines

Orphidis focuses on innovative therapies where treatment is specialist-led and patient identification, access and execution at the right treatment centres are critical. 

Therapeutic areas

Our therapeutic focus

Rare
Disease

Small, often underdiagnosed populations where patient identification and access are central.

Oncology / Hematology

Innovative cancer therapies delivered through specialist centres and hospital access pathways

Specialty
Medicines

Hospital-administered and high-value therapies where specialist prescribing and access determine uptake

Why specialist medicines require a different model

Concentrated patient populations

Patients may be treated in a limited number of specialist centres, making precision more important than commercial scale

Patient identification

Finding the right patients and understanding diagnosis and referral pathways can matter as much as product awareness

Complex access

Registration alone does not guarantee access. Reimbursement, private funding, hospital processes and named-patient pathways all influence how a medicine reaches patients

Focused execution

Resources go where they matter most: the centres, physicians and access pathways that determine treatment

Rare disease at scale

Rare diseases are individually uncommon but collectively affect a significant number of people.

~90–150M

People estimated to be living with a rare disease across our current market focus.

Estimate based on a global rare-disease prevalence of 3.5–5.9% applied to approximately 2.5 billion people. Sources: Nguengang Wakap et al., European Journal of Human Genetics (2020); UN World Population Prospects 2024. 

Let’s talk

Exploring a specialist medicine in Asia?

Whether you are considering managed access, registration or broader commercialisation, we’d welcome a conversation.